index - Repeat Expansions & Myotonic Dystrophy (REDs)

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CRISPRi Gene therapy Dystrophie Myotonique GABA KNOCKOUT MICE DM1 CTG repeats Motoneuron Thérapie génique Male CTG repeat instability Transcriptomics Alternative splicing Exercise Animals Cardiac muscle Mouse model BIOLOGIE MOLECULAIRE Diaphragm Myotonic dystrophy Brain Myotonic Dystrophy Type 1 Therapy PacBio Acute coronary syndrome Muscular dystrophy RNA interference Expression Myostatin Glutamate RNA biology Cell penetrating peptide Neuron Antisense oligonucleotides Gene Therapy Genotype phenotype correlation Astrocytes Humans Glucocorticoids Trinucleotide Repeat Expansion Centronuclear myopathy Myotonic Dystrophy type 1 Acetylcholinesterase deficiency Cell culture model Long read sequencing Glucocorticoid-receptor AAV ARN Intermediate filament Cell model Transgenic mouse model Dystrophie myotonique Myotonic Dystrophy Oligodendrocyte Endurance training Mice Dystrophin Skeletal muscle Maximal force Fibrosis Exercice Muscle CTG repeat contractions Mouse models ACETYLCHOLINESTERASE DMPK Heart Duchenne muscular dystrophy RNA splicing Cells Antisense oligonucleotide Myelin Central nervous system Hypoxia Aging Heart failure Gene editing GSK3␤ CRISPR/Cas9 Trinucleotide repeat expansion Transgenic mouse DMSXL mice MBNL Acetylcholinesterase knockout mouse CMS Dynamin 2 Astrocyte Myotonic dystrophy type 1 Brain dysfunction Cultured Desmin Oligodendrocytes CONGENITAL MYATHENIC SYNDROME Cytoskeleton Quantitative microdialysis Dilated cardiomyopathy Myotonic dystrophy mouse models PCR Glial cells Autophagy